Back

Notification report


Full notification file


General information

Notification Number
B/NL/20/017

Member State to which the notification was sent
Netherlands

Date of acknowledgement from the Member State Competent Authority
24/09/2020

Title of the Project
Phase I/II study of lentiviral gene transfer for SCID-X1

Proposed period of release:
01/01/2021 to 01/01/2030

Name of the Institute(s) or Company(ies)
Leiden University Medical Center, ;


3. Is the same GMO release planned elsewhere in the Community?
No

Has the same GMO been notified elsewhere by the same notifier?
No

GMO characterization

GMO is a:
Other: mammals

Identity of the GMO:
Autologous CD34+ hematopoietic stem cells transduced with a replication-deficient HIV-1 derived viral vector to transcribe and translate a correct form of therapeutic gene.

Information relating to the recipient or parental organisms from wich the GMO is derived
Common NameGenusSpeciesSubspeciesStrainPathovar
HumanHomoSapiens---

European Commission administrative information

Consent given by the Member State Competent Authority:
Yes
05/01/2021 00:00:00
Remarks: